Gene Therapy for Hemophilia: A Life-Changing Breakthrough

April 18, 2025

Gene therapy for hemophilia marks a revolutionary advancement in the treatment landscape for this inherited bleeding disorder, offering hope where traditional management has fallen short.Patients like Terence Blue, who recently became the first patient in New England to receive the FDA-approved therapy Hemgenix, are already experiencing remarkable benefits, including reduced reliance on frequent factor injections.
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